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H. Frangoul, MD, et al, AsCas12a gene editing of HBG1/2 promoters with EDIT-301 (reni-cel) results in rapid and sustained normalization of hemoglobin and increased fetal hemoglobin in patients with severe sickle cell disease and transfusion-dependent beta-thalassemia. Presented at the 2024 Tandem Meetings of ASTCT and CIBMTR. February 21-24, 2024.