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R. Hanna, M.D., et al. AsCas12a gene editing of HBG1/2 promoters with EDIT-301 results in rapid and sustained normalization of hemoglobin and increased fetal hemoglobin in patients with severe sickle cell disease and transfusion-dependent beta-thalassemia. Presented at the American Society of Hematology (ASH) Annual Meeting and Exposition. December 9-12, 2023.